Early screening for Duchenne muscular dystrophy can help you get early treatments and referrals for your child to help prevent further loss of muscle tissue. Duchenne muscular dystrophy (DMD ...

An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

Muscular Dystrophy Association and Burn Boot Camp Team Up for the 9th Annual 'Be Their Muscle' Philanthropic Event ...

Dec. 16, 2024 — A novel drug holds promise for treating Duchenne muscular dystrophy (DMD), a rare genetic disorder that causes severe muscle degeneration. Researchers have discovered that an ...

New research led by the University of Portsmouth has revealed how Duchenne muscular dystrophy (DMD), best known for causing severe muscle degeneration, also profoundly affects the brain ...

Cambridge, Mass.-based Sarepta Therapeutics reported the first known death from its Duchenne muscular dystrophy gene therapy ...

Participants in the FORWARD-53 trial had clinically significant improvements in time-to-rise, among other metrics.

One of the major highlights of the Muscular Dystrophy Association (MDA) Clinical & Scientific Conference is that invaluable ...

A team has discovered a possible therapeutic approach to repair injured muscles either from aging or degenerative muscle disorders.

Avidity Biosciences Inc. says will submit an application for accelerated approval to the FDA for del-zota before the end of ...