An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

Early screening for Duchenne muscular dystrophy can help you get early treatments and referrals for your child to help prevent further loss of muscle tissue. Duchenne muscular dystrophy (DMD ...

WVE-N531, an oligonucleotide, elicited significant functional benefit and reversal of muscle damage in the Phase II ...

Treatment with losmapimod resulted in no clear benefit compared with placebo in individuals with facioscapulohumeral muscular dystrophy at 48 weeks, according to research presented at MDA.

The startup is using CRISPR tools to stop errant expression of a gene linked to facioscapulohumeral muscular dystrophy, a ...

New research led by the University of Portsmouth has revealed how Duchenne muscular dystrophy (DMD), best known for causing severe muscle degeneration, also profoundly affects the brain ...

Dec. 16, 2024 — A novel drug holds promise for treating Duchenne muscular dystrophy (DMD), a rare genetic disorder that causes severe muscle degeneration. Researchers have discovered that an ...

Duchenne muscular dystrophy (DMD) is a disorder that causes progressive muscle weakness and a loss of function. The symptoms appear early in life, and most affected individuals require the use of ...

WVE-N531 demonstrated statistically significant improvements in muscle biopsy measures and functional measures in patients ...

A PhD student with limb girdle muscular dystrophy will be the official race starter for this year's Oxford 10k.