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The Texas Coalition for Patients has a legislative priority list that includes restrictions on artificial intelligence and ...

Discover how small biotechs are innovating in the weight loss therapy market with new treatments targeting unique mechanisms ...

Liver issues, including a buildup of fat in the liver, occur before the onset of neuromuscular disease, per a study in a mouse model of SMA.

Infants with SMA type 1 born since 2016 experience better functional outcomes and life expectancy with disease-modifying treatments.

A new electrical stimulation therapy for spinal muscle atrophy (SMA) has shown promise in reactivating motor neurons and ...

For columnist Alyssa Silva, advances in the development of SMA treatments have felt like glimmers of miracles.

Three patients with spinal muscular atrophy had improved muscle strength and could walk farther after a month of daily spinal ...

Three patients with spinal muscular atrophy had improved muscle strength and could walk farther after a month of daily spinal ...

Describe how imaging and the use of new therapies for geographic atrophy secondary to age-related macular degeneration can fit into the treatment paradigm. Summarize innovations in imaging that ...

Australia's Therapeutic Goods Administration has approved the use of a new and first treatment for geographic atrophy - a disease which causes severe, progressive central vision loss and is a leading ...

Roche has announced positive results from the Phase III EMBARK clinical trial of Elevidys (delandistrogene moxeparvovec) for the treatment of Duchenne muscular dystrophy (DMD). Following two years of ...