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The exceptionally rare disease that causes holes to form in your brain
Creutzfeldt-Jakob disease is an extremely rare and fatal brain-wasting disease that's like a human version of "mad cow." ...
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Rare Diseases Are Neglected. The FDA Needs A Dedicated 'Center of Excellence for Rare Diseases'.
The FDA has made some modest efforts, but it needs an internal organization that understands and would be an aggressive ...
News Medical on MSN2d
AI approach reveals possible fusion of rare diseases in COVID-19 origins In A Landmark Dis...
Despite extensive research, the origins of COVID-19 remain elusive. In a new study published in the KeAi journal Advances in Biomarker Sciences and Technology (ABST), an AI-driven approach was adopted ...
‘Noah,' a Documentary About a Woman With Seven Rare and Incurable Diseases, Acquired by Jambika Docs (EXCLUSIVE)
Barcelona-based sales agency Jambika Docs has acquired the documentary feature "Noah" ahead of the European Film Market in ...
EurekAlert!3d
Uncovering two rare infectious diseases which might be responsible for COVID-19
In a landmark discovery, researchers applied a novel AI model called the max-logistic intelligence classifier to analyze ...
STAT7d
What happens when a rare disease drug seems to work, but the health care system doesn’t?
Cristina Brennan can hear the clock ticking. At the end of the year, her 12-year-old son Tristan will no longer have free ...
GlobalData on MSN23h
Travere takes rare disease kidney drug to FDA despite failed trial
Travere’s stock price climbed by 14% following the announcement that it will seek an FDA label expansion for Filspari.
FiercePharma23h
Amid takeover talk, SpringWorks scores FDA nod for rare genetic disease treatment Gomekli
Tuesday, the agency signed off on SpringWorks’ Gomekli (mirdametinib) as a treatment for the rare genetic disorder ...
AI predicts effective treatment for rare disease using existing medications
After combing through 4,000 existing medications, an artificial intelligence tool helped uncover one that saved the life of a patient with idiopathic multicentric Castleman's disease (iMCD).
Foodborne botulism is a rare, life-threatening condition. These are the signs to look for.
Canned foods are often the culprit of this rare, but potentially deadly, condition. The good news is: It's treatable if ...
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Mfantsipim Old Boy Who Has Been Standing For 5 Years Opens Up About Rare Disease
A first-year University of Cape Coast student and Mfantsipim old boy, Enock Eshun has been battling a rare disease that has ...
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Texarkana boy battling rare disease prepares for life-changing transplant
TEXARKANA, Texas - A Texarkana, Texas boy battling a rare genetic disease is preparing to head to Arkansas Children's ...