Recordati CEO Rob Koremans joined "Squawk Box Europe" after the pharmaceutical company raised its 2025 revenue and core profit forecasts by more than expected, seeing strong demand for its rare ...
Your genes play a huge role in what makes and shapes your entire existence. Since you inherit your genes from your parents, ...
A combination of human pedigree analysis and fruit fly genetics has identified a gene variant that appears to prevent PIGA-CDG, a rare but serious seizure disorder. The findings could ultimately lead ...
According to his parents, Eli is a “miracle baby,” surviving multiple hurdles since birth. Tune in TONIGHT at 5:00 p.m. to hear his story.
A young girl with a rare disease is preparing for a lengthy road to recovery. She’s hoping to decorate her hospital room with ...
Ascendis Pharma beat Q4 earnings and revenue estimates, driven by a $100M Novo Nordisk deal and Yorvipath's EU launch.
Researchers provided a long-awaited and rare genetic diagnosis in a child with Lennox-Gastaut syndrome, a type of ...
Five years ago, the COVID-19 pandemic served as a wake-up call. Since then, health experts worldwide have sat on tenterhooks, ...
February is Rare Disease Month, an annual effort to highlight the challenges families can face while navigating rare ...
Soil and water tests confirm workers in Ventura County raspberry fields were infected by the rare disease leptospirosis.
The event featured not only Austin Laurette, who is "the unbreakable boy," but also some of the stars of the movie, Zachary ...
Its architect's daughter has cystic fibrosis—and benefits from a "miracle drug" backed by an agency he's attacking.