ET HealthWorld2d
Parents of muscular dystrophic patients protest in Delhi, demand access to high-cost treatment
One of the demands raised during the protests was access to 'Elevidys', a one-time gene therapy treatment that has the ...
Managed Healthcare Executive2d
Caregiver Burden and Value Assessments in Duchenne Muscular Dystrophy
Doing more to incorporate caregiver burden into value assessments and cost-effectiveness research of Duchene muscular dystrophy treatments was the focus of a recent International Society for ...
A mother’s battle: Advocating for life-saving treatments for children with Duchenne muscular dystrophy
When her son reached three last year, a new name loomed over their lives — Duchenne Muscular Dystrophy (DMD), a ...
Sarepta/Roche Suspend Elevidys Gene Therapy Trials In Europe After Patient Death
Sarepta Therapeutics, Inc. (NASDAQ:SRPT) shared an update on Elevidys (delandistrogene moxeparvovec-rokl), the only approved ...
Managed Healthcare Executive4d
Wave’s Duchenne Therapy Has Promising Phase 2 Results
Participants in the FORWARD-53 trial had clinically significant improvements in time-to-rise, among other metrics.
Defeat Duchenne Canada Launches 2025 Research Grant Cycle, Set to Commit its $20 Millionth Dollar to Groundbreaking Research
Defeat Duchenne Canada, the country's leading funder of Duchenne muscular dystrophy (DMD) research, is set to begin accepting innovative research proposals as of March 31, 2025. They are seeking ...
Muscular Dystrophy Association and Burn Boot Camp Team Up for the 9th Annual ‘Be Their Muscle’ Philanthropic Event
Muscular Dystrophy Association (MDA) has teamed up with Burn Boot Camp, a leading boutique fitness franchise, for the 9th annual national 'Be Their Muscle' philanthropic event. Throughout April, over ...
Scottish family leave for US to give terminally ill boy 'fighting chance' with treatment
Parents Jamie, 33, and Bobbie, 32, have spent the last three years desperately seeking treatments abroad and have been ...
Hindustan Times2d
Parents of muscular dystrophic patients protest in Delhi, demand access to high-cost treatment
who are unable to access critical treatments due to their exorbitant costs, the statement said. Duchenne Muscular Dystrophy is a genetic disorder characterised by progressive muscle degeneration ...