Despite significant advancements in spinal muscular atrophy (SMA) management, unmet needs persist, especially for patients ...

FDA-approved treatments for spinal muscular atrophy differ in their mechanisms of action, safety profiles, and administration challenges, with key selection factors like patient age and gene copy ...

The NIH is considering a catastrophic cut to indirect cost reimbursements for public universities, which would hurt the ...

Freddie-Shaun Dahill Egan was born with spinal muscular atrophy (SMA), a rare genetic condition that causes progressive ...

Javed Shaikh, Director of RWE & HEOR, Axtria, explains how harnessing next-generation sequencing and AI-powered analytics ...

Funding medical research is about more than just numbers. It's real people,” says Ryan Manriquez, president of the UC ...

Affordable generic version of SMA drug Risdiplam soon available in India, offering hope to patients and activists.

Natco Pharma updates on Risdiplam launch in India, Delhi High Court denies Roche's injunction plea, pricing set at ₹15,900.