Examples include Exondys 51 (eteplirsen ... What foods should you avoid with muscular dystrophy? People with muscular ...

An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

Adeno-associated virus (AAV)–mediated gene therapy was one of the focal points of this year's Muscular Dystrophy Association conference. Here, Barry Byrne, MD, PhD, University of Florida, speaks to ...

Learning from examples like congenital heart disease and cystic fibrosis can help health systems and clinicians prepare to care for an influx of patients with neuromuscular diseases as they reach ...

Dec. 16, 2024 — A novel drug holds promise for treating Duchenne muscular dystrophy (DMD), a rare genetic disorder that causes severe muscle degeneration. Researchers have discovered that an ...

This story is republished from STAT, the health and medicine news site that’s a partner to the Globe. Sign up for STAT’s free Morning Rounds newsletter here. Wave Life Sciences’ experimental ...

Cambridge, Mass.-based Sarepta Therapeutics reported the first known death from its Duchenne muscular dystrophy gene therapy ...

While plenty of people are going green in honor of Saint Patrick's Day, one student at East Stroudsburg University is turning ...

The young man died of acute liver injury, a known side effect, Sarepta said in a statement. But the company said the ...

Considering taking supplements to treat muscular dystrophy? Below is a list of common natural remedies used to treat or reduce the symptoms of muscular dystrophy. Follow the links to read common ...

Duchenne muscular dystrophy causes progressive muscle degeneration ... The consensus committee specifically names swimming and cycling as examples of acceptable low impact exercises, but those ...