Duchenne muscular dystrophy causes progressive muscle degeneration ... The consensus committee specifically names swimming and cycling as examples of acceptable low impact exercises, but those ...

An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

Learning from examples like congenital heart disease and cystic fibrosis can help health systems and clinicians prepare to care for an influx of patients with neuromuscular diseases as they reach ...

Cambridge, Mass.-based Sarepta Therapeutics reported the first known death from its Duchenne muscular dystrophy gene therapy ...

Researchers from Suzhou Genassist Therapeutics Co. Ltd. have developed a novel canine model of Duchenne muscular dystrophy (DMD), expected to be more predictive of disease pathogenesis and treatment ...

Adeno-associated virus (AAV)–mediated gene therapy was one of the focal points of this year's Muscular Dystrophy Association conference. Here, Barry Byrne, MD, PhD, University of Florida, speaks to ...

The young man died of acute liver injury, a known side effect, Sarepta said in a statement. But the company said the ...

While plenty of people are going green in honor of Saint Patrick's Day, one student at East Stroudsburg University is turning ...