Northern Minnesota boy is first American to receive groundbreaking treatment for muscular dystrophy
An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.
Patient dies following muscular dystrophy gene therapy, Sarepta reports
A patient has died while taking a closely watched gene therapy for muscular dystrophy. Sarepta Therapeutics announced the ...
Capricor Therapeutics Announces Positive Data Demonstrating Long-Term Efficacy of Deramiocel for the Treatment of Duchenne Muscular Dystrophy
Preservation of Skeletal Muscle Function Shown Over 3 Years Resulting in 52% Slowing of Disease-- --Data Presented at the ...
The American Journal of Managed Care10d
Regenerating Neurons, Muscle, and Hope in the Field of Muscular Dystrophy
Muscular Dystrophy Association Clinical & Scientific Conference, convening in Dallas, Texas, from March 16-18, will feature ...
American Association of Individual Investors3d
Why Capricor Therapeutics, Inc.’s (CAPR) Stock Is Down 10.45%
Capricor Therapeutics, Inc.’s CAPR share price has dipped by 10.45%, which has investors questioning if this is right time to ...
STAT7d
AstraZeneca buys European cell therapy company
From STAT’s Andrew Joseph: AstraZeneca said this morning it was buying the Belgian cell therapy company EsoBiotec for $425 million upfront, building out another cancer-targeting approach.
The American Journal of Managed Care6d
Shaping Gene Therapy Approaches in Neuromuscular Disease
Adeno-associated virus (AAV)–mediated gene therapy was one of the focal points of this year's Muscular Dystrophy Association conference. Here, Barry Byrne, MD, PhD, University of Florida, speaks to ...
KESQ News2d
Boy is first American to receive groundbreaking treatment for muscular dystrophy
“This spreads around and gets into the muscle cells,” said Karachunski ... Karachunski said there are many more muscular dystrophy treatments that are currently in clinical trials that ...